Browse by UCL people
Group by: Type | Date
Number of items: 24.
Article
Baruteau, J;
Cunningham, SC;
Yilmaz, BS;
Perocheau, DP;
Eaglestone, S;
Burke, D;
Thrasher, AJ;
... Gissen, P; + view all
(2021)
Safety and efficacy of an engineered hepatotropic AAV gene therapy for ornithine transcarbamylase deficiency in cynomolgus monkeys.
Molecular Therapy - Methods & Clinical Development
, 23
pp. 135-146.
10.1016/j.omtm.2021.09.005.
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Baruteau, J;
Perocheau, DP;
Hanley, J;
Lorvellec, M;
Rocha-Ferreira, E;
Karda, R;
Ng, J;
... Waddington, SN; + view all
(2018)
Argininosuccinic aciduria fosters neuronal nitrosative stress reversed by Asl gene transfer.
Nature Communications
, 9
(1)
, Article 3505. 10.1038/s41467-018-05972-1.
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Buckley, SM;
Delhove, JM;
Perocheau, DP;
Karda, R;
Rahim, AA;
Howe, SJ;
Ward, NJ;
... McKay, TR; + view all
(2015)
In vivo bioimaging with tissue-specific transcription factor activated luciferase reporters.
Scientific Reports
, 5
, Article 11842. 10.1038/srep11842.
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Counsell, JR;
De Brabandere, G;
Karda, R;
Moore, M;
Greco, A;
Bray, A;
Diaz, JA;
... Waddington, SN; + view all
(2021)
Re-structuring lentiviral vectors to express genomic RNA via cap-dependent translation.
Molecular Therapy - Methods and Clinical Development
, 20
pp. 357-365.
10.1016/j.omtm.2020.12.005.
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Delhove, JM;
Buckley, SM;
Perocheau, DP;
Karda, R;
Arbuthnot, P;
Henderson, NC;
Waddington, SN;
(2017)
Longitudinal in vivo bioimaging of hepatocyte transcription factor activity following cholestatic liver injury in mice.
Scientific Reports
, 7
, Article 41874. 10.1038/srep41874.
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Gurung, S;
Perocheau, D;
Touramanidou, L;
Baruteau, J;
(2021)
The exosome journey: from biogenesis to uptake and intracellular signalling.
Cell Communication and Signaling
, 19
(1)
, Article 47. 10.1186/s12964-021-00730-1.
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Huang, YS;
Tseng, WY;
Clanchy, FIL;
Topping, LM;
Ogbechi, J;
McNamee, K;
Perocheau, D;
... Williams, RO; + view all
(2021)
Pharmacological modulation of T cell immunity results in long-term remission of autoimmune arthritis.
Proceedings of the National Academy of Sciences of the United States of America
, 118
(19)
, Article e2100939118. 10.1073/pnas.2100939118.
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Karda, R;
Perocheau, DP;
Suff, N;
Ng, J;
Delhove, JMKM;
Buckley, SMK;
Richards, S;
... Waddington, SN; + view all
(2017)
Continual conscious bioluminescent imaging in freely moving somatotransgenic mice.
Sci Rep
, 7
(1)
, Article 6374. 10.1038/s41598-017-06696-w.
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Karda, R;
Rahim, AA;
Wong, AMS;
Suff, N;
Diaz, JA;
Perocheau, DP;
Tijani, M;
... Waddington, SN; + view all
(2020)
Generation of light-producing somatic-transgenic mice using adeno-associated virus vectors.
Scientific Reports
, 10
(1)
, Article 2121. 10.1038/s41598-020-59075-3.
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Lorvellec, M;
Pellegata, AF;
Maestri, A;
Turchetta, C;
Alvarez Mediavilla, E;
Shibuya, S;
Jones, B;
... Gissen, P; + view all
(2020)
An In Vitro Whole-Organ Liver Engineering for Testing of Genetic Therapies.
iScience
, 23
(12)
, Article 101808. 10.1016/j.isci.2020.101808.
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Massaro, G;
Mattar, CNZ;
Wong, AMS;
Sirka, E;
Buckley, SMK;
Herbert, BR;
Karlsson, S;
... Rahim, AA; + view all
(2018)
Fetal gene therapy for neurodegenerative disease of infants.
Nature Medicine
, 24
pp. 1317-1323.
10.1038/s41591-018-0106-7.
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Ng, J;
Barral, S;
Barrigon, CDLF;
Lignani, G;
Erdem, FA;
Wallings, R;
Privolizzi, R;
... Kurian, MA; + view all
(2021)
Gene therapy restores dopamine transporter expression and ameliorates pathology in iPSC and mouse models of infantile parkinsonism.
Science Translational Medicine
, 13
(594)
, Article eaaw1564. 10.1126/scitranslmed.aaw1564.
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Nivsarkar, MS;
Buckley, SM;
Parker, AL;
Perocheau, D;
McKay, TR;
Rahim, AA;
Howe, SJ;
(2015)
Evidence for Contribution of CD4+CD25+ Regulatory T Cells in Maintaining Immune Tolerance to Human Factor IX following Perinatal Adenovirus Vector Delivery.
Journal of Immunology Research
, 2015
, Article 397879. 10.1155/2015/397879.
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Perocheau, Dany;
Duff, Claire;
Gurung, Sonam;
Touramanidou, Loukia;
Sharma, Garima;
Baruteau, Julien;
(2024)
Optimized and Simplified Technique for the Production and Culture of Precision-Cut Liver Slices.
Journal of Visualized Experiments (JoVE)
, 213
, Article e67202. 10.3791/67202.
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Perocheau, D;
Cunningham, S;
Lee, J;
Antinao Diaz, J;
Waddington, SN;
Gilmour, K;
Eaglestone, S;
... Baruteau, J; + view all
(2019)
Age-Related Seroprevalence of Antibodies Against AAV-LK03 in a UK Population Cohort.
Human Gene Therapy
, 30
(1)
pp. 79-87.
10.1089/hum.2018.098.
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Perocheau, D;
Touramanidou, L;
Gurung, S;
Gissen, P;
Baruteau, J;
(2021)
Clinical applications for exosomes: are we there yet?
British Journal of Pharmacology
10.1111/bph.15432.
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Plotegher, N;
Perocheau, D;
Ferrazza, R;
Massaro, G;
Bhosale, G;
Zambon, F;
Rahim, AA;
... Duchen, MR; + view all
(2020)
Impaired cellular bioenergetics caused by GBA1 depletion sensitizes neurons to calcium overload.
Cell Death & Differentiation
, 27
pp. 1588-1603.
10.1038/s41418-019-0442-2.
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Soria, LR;
Gurung, S;
De Sabbata, G;
Perocheau, D;
De Angelis, A;
Bruno, G;
Polishchuk, E;
... Brunetti-Pierri, N; + view all
(2020)
Beclin‐1‐mediated activation of autophagy improves proximal and distal urea cycle disorders.
EMBO Molecular Medicine
, Article e13158. 10.15252/emmm.202013158.
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Suff, N;
Karda, R;
Antinao Diaz, J;
Ng, J;
Baruteau, J;
Perocheau, D;
Tangney, M;
... Waddington, SN; + view all
(2018)
Ascending Vaginal Infection Using Bioluminescent Bacteria Evokes Intrauterine Inflammation, Preterm Birth and Neonatal Brain Injury in Pregnant Mice.
American Journal of Pathology
, 188
(10)
pp. 2164-2176.
10.1016/j.ajpath.2018.06.016.
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Suff, N;
Rajvinder, K;
Diaz, A;
Ng, J;
Baruteau, J;
Perocheau, D;
Taylor, P;
... Peebles, DM; + view all
(2020)
Cervical gene delivery of the antimicrobial peptide, Human β‐defensin (HBD)-3, in a mouse model of ascending infection-related preterm birth.
Frontiers in Immunology
, 11
, Article 106. 10.3389/fimmu.2020.00106.
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Touramanidou, Loukia;
Gurung, Sonam;
Cozmescu, Claudiu A;
Perocheau, Dany;
Moulding, Dale;
Finn, Patrick F;
Frassetto, Andrea;
... Baruteau, Julien; + view all
(2024)
Macrophage Inhibitor Clodronate Enhances Liver Transduction of Lentiviral but Not Adeno-Associated Viral Vectors or mRNA Lipid Nanoparticles in Neonatal and Juvenile Mice.
Cells
, 13
(23)
, Article 1979. 10.3390/cells13231979.
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Vink, CA;
Counsell, JR;
Perocheau, DP;
Karda, R;
Buckley, SMK;
Brugman, MH;
Galla, M;
... Howe, SJ; + view all
(2017)
Eliminating HIV-1 Packaging Sequences from Lentiviral Vector Proviruses Enhances Safety and Expedites Gene Transfer for Gene Therapy.
Molecular Therapy
, 25
(8)
pp. 1790-1804.
10.1016/j.ymthe.2017.04.028.
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Proceedings paper
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Karda, R;
Perocheau, DP;
Suff, N;
Ng, J;
Hughes, M;
Rahim, AA;
Buckley, SMK;
... Waddington, SN; + view all
(2016)
Generation of light-producing somatic-transgenic mice using adeno-associated virus vectors.
In:
Human Gene Therapy. November 2016, 27(11).
(pp. A107-A108).
Mary Ann Liebert, Inc
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Thesis
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Sundaram, V;
(2014)
Gene therapy for inherited retinal diseases.
Doctoral thesis , UCL (University College London).
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