Browse by UCL people
Group by: Type | Date
Jump to: Article
Number of items: 3.
Article
Piras, G;
Montiel-Equihua, C;
Chan, Y-KA;
Wantuch, S;
Stuckey, D;
Burke, D;
Prunty, H;
... Gaspar, HB; + view all
(2020)
Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease.
Molecular Therapy - Methods and Clinical Development
, 18
pp. 558-570.
10.1016/j.omtm.2020.07.001.
|
Rattazzi, L;
Piras, G;
Brod, S;
Smith, K;
Ono, M;
D'Acquisto, F;
(2016)
Impact of Enriched Environment on Murine T Cell Differentiation and Gene Expression Profile.
Frontiers in Immunology
, 7
, Article 381. 10.3389/fimmu.2016.00381.
|
Schejtman, A;
Vetharoy, W;
Choi, U;
Rivat, C;
Theobald, N;
Piras, G;
Leon-Rico, D;
... Santilli, G; + view all
(2021)
Preclinical Optimization and Safety Studies of a New Lentiviral Gene Therapy for p47phox-Deficient Chronic Granulomatous Disease.
Human Gene Therapy
, 32
(17-18)
pp. 949-958.
10.1089/hum.2020.276.
|