Browse by UCL people
Group by: Type | Date
Number of items: 6.
Article
Kohn, DB;
Booth, C;
Kang, EM;
Pai, S-Y;
Shaw, KL;
Santilli, G;
Armant, M;
... the Net4CGD consortium; + view all
(2020)
Lentiviral gene therapy for X-linked chronic granulomatous disease.
Nature Medicine
, 26
pp. 200-206.
10.1038/s41591-019-0735-5.
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Leon-Rico, D;
Aldea, M;
Sanchez-Baltasar, R;
Mesa-Nuñez, C;
Record, J;
Burns, SO;
Santilli, G;
... Almarza, E; + view all
(2016)
Lentiviral Vector-Mediated Correction of a Mouse Model of Leukocyte Adhesion Deficiency Type I.
Human Gene Therapy
, 27
(9)
pp. 668-678.
10.1089/hum.2016.016.
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Mesa-Núñez, C;
Leon-Rico, D;
Aldea, M;
Damián, C;
Sanchez-Baltasar, R;
Sanchez, R;
Alberquilla, O;
... Almarza, E; + view all
(2020)
The downregulated membrane expression of CD18 in CD34+ cells defines a primitive population of human hematopoietic stem cells.
Stem Cell Research & Therapy
, 11
, Article 164. 10.1186/s13287-020-01672-0.
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Piras, G;
Montiel-Equihua, C;
Chan, Y-KA;
Wantuch, S;
Stuckey, D;
Burke, D;
Prunty, H;
... Gaspar, HB; + view all
(2020)
Lentiviral Hematopoietic Stem Cell Gene Therapy Rescues Clinical Phenotypes in a Murine Model of Pompe Disease.
Molecular Therapy - Methods and Clinical Development
, 18
pp. 558-570.
10.1016/j.omtm.2020.07.001.
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Schott, JW;
León-Rico, D;
Ferreira, CB;
Buckland, KF;
Santilli, G;
Armant, MA;
Schambach, A;
... Thrasher, AJ; + view all
(2019)
Enhancing Lentiviral and Alpharetroviral Transduction of Human Hematopoietic Stem Cells for Clinical Application.
Molecular Therapy - Methods and Clinical Development
, 14
pp. 134-147.
10.1016/j.omtm.2019.05.015.
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Poster
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Schott, JW;
Leon-Rico, D;
Armenteros-Monterroso, E;
Buckland, KF;
Rivat, C;
Disakou, A;
Pereira, I;
... Thrasher, AJ; + view all
(2018)
Systematic comparison of culture media and transduction enhancers for optimised CD34⁺ cell-based retroviral gene therapy protocols.
Presented at: Changing the Face of Modern Medicine: Stem Cells & Gene Therapy, Lausanne, Switzerland.
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