Michaelides, M;
Besirli, CG;
Bainbridge, J;
(2025)
A plain language summary of the phase 1/2 study of AAV5-hRKp.RPGR (botaretigene sparoparvovec) in people with RPGR-associated X-linked retinitis pigmentosa.
Future Rare Diseases
, 5
(1)
, Article 2535273. 10.1080/23995270.2025.2535273.
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A plain language summary of the phase 1 2 study of AAV5-hRKp.RPGR botaretigene sparoparvovec in people with RPGR-associated X-linked retinitis pigme.pdf - Published Version Download (2MB) | Preview |
| Type: | Article |
|---|---|
| Title: | A plain language summary of the phase 1/2 study of AAV5-hRKp.RPGR (botaretigene sparoparvovec) in people with RPGR-associated X-linked retinitis pigmentosa |
| Open access status: | An open access version is available from UCL Discovery |
| DOI: | 10.1080/23995270.2025.2535273 |
| Publisher version: | https://doi.org/10.1080/23995270.2025.2535273 |
| Language: | English |
| Additional information: | © 2025 The Author(s). Published by Informa UK Limited, trading as Taylor & Francis Group This is an Open Access article distributed under the terms of the Creative Commons Attribution-NonCommercial License (http://creativecommons.org/licenses/by-nc/4.0/), which permits unrestricted non-commercial use, distribution, and reproduction in any medium, provided the original work is properly cited. The terms on which this article has been published allow the posting of the Accepted Manuscript in a repository by the author(s) or with their consent. |
| UCL classification: | UCL UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences > Institute of Ophthalmology |
| URI: | https://discovery.ucl.ac.uk/id/eprint/10212309 |
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