UCL Discovery
UCL home » Library Services » Electronic resources » UCL Discovery

Proof-of-concept for multiple AON delivery by a single U7snRNA vector to restore splicing defects in ABCA4

Suárez-Herrera, Nuria; Riswick, Iris B; Vázquez-Domínguez, Irene; Duijkers, Lonneke; Karjosukarso, Dyah W; Piccolo, Davide; Bauwens, Miriam; ... Collin, Rob WJ; + view all (2024) Proof-of-concept for multiple AON delivery by a single U7snRNA vector to restore splicing defects in ABCA4. Molecular Therapy 10.1016/j.ymthe.2024.01.019. (In press).

[thumbnail of 1-s2.0-S1525001624000194-main.pdf] Text
1-s2.0-S1525001624000194-main.pdf - Accepted Version
Access restricted to UCL open access staff until 27 July 2024.

Download (7MB)
Type: Article
Title: Proof-of-concept for multiple AON delivery by a single U7snRNA vector to restore splicing defects in ABCA4
Location: United States
DOI: 10.1016/j.ymthe.2024.01.019
Publisher version: https://doi.org/10.1016/j.ymthe.2024.01.019
Language: English
Additional information: This version is the author accepted manuscript. For information on re-use, please refer to the publisher's terms and conditions.
UCL classification: UCL
UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences
UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences
UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences > Institute of Ophthalmology
URI: https://discovery.ucl.ac.uk/id/eprint/10186131
Downloads since deposit
1Download
Download activity - last month
Download activity - last 12 months
Downloads by country - last 12 months

Archive Staff Only

View Item View Item