Welsh, NJ;
Gewinner, CA;
Mistry, K;
Koglin, M;
Cooke, J;
Butler, M;
Powney, B;
... Schapira, AHV; + view all
(2019)
Functional assessment of glucocerebrosidase modulator efficacy in primary patient-derived macrophages is essential for drug development and patient stratification.
Haematologica
10.3324/haematol.2019.224717.
(In press).
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Type: | Article |
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Title: | Functional assessment of glucocerebrosidase modulator efficacy in primary patient-derived macrophages is essential for drug development and patient stratification. |
Location: | Italy |
Open access status: | An open access version is available from UCL Discovery |
DOI: | 10.3324/haematol.2019.224717 |
Publisher version: | http://doi.org/10.3324/haematol.2019.224717 |
Language: | English |
Additional information: | This version is the author accepted manuscript. For information on re-use, please refer to the publisher’s terms and conditions. |
Keywords: | Gaucher Disease, Granulocytes, Monocytes, Macrophages, Molecular Pharmacology, pharmacological chaperone |
UCL classification: | UCL UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences > UCL Queen Square Institute of Neurology UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences > UCL Queen Square Institute of Neurology > Clinical and Movement Neurosciences |
URI: | https://discovery.ucl.ac.uk/id/eprint/10082992 |
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