Welsh, NJ;
              
      
            
                Gewinner, CA;
              
      
            
                Mistry, K;
              
      
            
                Koglin, M;
              
      
            
                Cooke, J;
              
      
            
                Butler, M;
              
      
            
                Powney, B;
              
      
            
            
          
      
            
            
          
      
            
            
            ... Schapira, AHV; + view all
            
          
      
        
        
        
    
  
(2019)
  Functional assessment of glucocerebrosidase modulator efficacy in primary patient-derived macrophages is essential for drug development and patient stratification.
Haematologica
      
    
    
    
         10.3324/haematol.2019.224717.
   (In press).
  
      
    
  
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| Type: | Article | 
|---|---|
| Title: | Functional assessment of glucocerebrosidase modulator efficacy in primary patient-derived macrophages is essential for drug development and patient stratification. | 
| Location: | Italy | 
| Open access status: | An open access version is available from UCL Discovery | 
| DOI: | 10.3324/haematol.2019.224717 | 
| Publisher version: | http://doi.org/10.3324/haematol.2019.224717 | 
| Language: | English | 
| Additional information: | This version is the author accepted manuscript. For information on re-use, please refer to the publisher’s terms and conditions. | 
| Keywords: | Gaucher Disease, Granulocytes, Monocytes, Macrophages, Molecular Pharmacology, pharmacological chaperone | 
| UCL classification: | UCL UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences > UCL Queen Square Institute of Neurology UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Brain Sciences > UCL Queen Square Institute of Neurology > Clinical and Movement Neurosciences  | 
        
| URI: | https://discovery.ucl.ac.uk/id/eprint/10082992 | 
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