Debnath, S;
Jaako, P;
Siva, K;
Rothe, M;
Chen, J;
Dahl, M;
Gaspar, HB;
... Karlsson, S; + view all
(2017)
Lentiviral Vectors with Cellular Promoters Correct Anemia and Lethal Bone Marrow Failure in a Mouse Model for Diamond-Blackfan Anemia.
Molecular Therapy
, 25
(8)
pp. 1805-1814.
10.1016/j.ymthe.2017.04.002.