Miller, JRC;
Pfister, EL;
Liu, W;
Andre, R;
Träger, U;
Kennington, LA;
Lo, K;
... Tabrizi, SJ; + view all
(2017)
Allele-Selective Suppression of Mutant Huntingtin in Primary Human Blood Cells.
Scientific Reports
, 7
, Article 46740. 10.1038/srep46740.