Godfrey, C;
Desviat, LR;
Smedsrød, B;
Piétri-Rouxel, F;
Denti, MA;
Disterer, P;
Lorain, S;
... Arechavala-Gomeza, V; + view all
(2017)
Delivery is key: lessons learnt from developing splice-switching antisense therapies.
EMBO Molecular Medicine
, 9
(3)
pp. 281-394.
10.15252/emmm.201607199.