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Nicholls, K;
Shankar, SP;
Sunder-Plassmann, G;
Koeller, D;
Nedd, K;
Vockley, G;
... Feldt-Rasmussen, U; + view all
(2017)
Oral pharmacological chaperone migalastat compared with enzyme replacement therapy in Fabry disease: 18-month results from the randomised phase III ATTRACT study.
Journal of Medical Genetics
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pp. 288-296.
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