Valayannopoulos, V;
Baruteau, J;
Delgado, MB;
Cano, A;
Couce, ML;
Del Toro, M;
Donati, MA;
... Chakrapani, A; + view all
(2016)
Carglumic acid enhances rapid ammonia detoxification in classical organic acidurias with a favourable risk-benefit profile: A retrospective observational study.
Orphanet Journal of Rare Diseases
, 11
, Article 32. 10.1186/s13023-016-0406-2.