?url_ver=Z39.88-2004&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Ajournal&rft.aufirst=John+K&rft.au=Yoon%2C+John+K&rft.aulast=Yoon&rft.atitle=Preclinical+lentiviral+vector-mediated+hematopoietic+stem+and+progenitor+cell+gene+therapy+corrects+Pompe+disease-related+muscle+and+neurological+manifestations&rft.date=17+September+2024&rft.title=Molecular+Therapy&rft.genre=article