eprintid: 10184217 rev_number: 7 eprint_status: archive userid: 699 dir: disk0/10/18/42/17 datestamp: 2023-12-20 09:44:06 lastmod: 2023-12-20 09:44:06 status_changed: 2023-12-20 09:44:06 type: article metadata_visibility: show sword_depositor: 699 creators_name: Uras, Giuseppe creators_name: Li, Xinuo creators_name: Manca, Alessia creators_name: Pantaleo, Antonella creators_name: Bo, Marco creators_name: Xu, Jinyi creators_name: Allen, Stephanie creators_name: Zhu, Zheying title: Development of p-Tau Differentiated Cell Model of Alzheimer’s Disease to Screen Novel Acetylcholinesterase Inhibitors ispublished: pub divisions: UCL divisions: B02 divisions: C07 divisions: D07 divisions: F84 keywords: Alzheimer; AChE; GSK3-β; inhibitors; Tau; hyperphosphorylation note: Copyright © 2022 by the authors. Licensee MDPI, Basel, Switzerland. This article is an open access article distributed under the terms and conditions of the Creative Commons Attribution (CC BY) license (https://creativecommons.org/licenses/by/4.0/). abstract: Alzheimer’s disease (AD) is characterized by an initial accumulation of amyloid plaques and neurofibrillary tangles, along with the depletion of cholinergic markers. The currently available therapies for AD do not present any disease-modifying effects, with the available in vitro platforms to study either AD drug candidates or basic biology not fully recapitulating the main features of the disease or being extremely costly, such as iPSC-derived neurons. In the present work, we developed and validated a novel cell-based AD model featuring Tau hyperphosphorylation and degenerative neuronal morphology. Using the model, we evaluated the efficacy of three different groups of newly synthesized acetylcholinesterase (AChE) inhibitors, along with a new dual acetylcholinesterase/glycogen synthase kinase 3 inhibitor, as potential AD treatment on differentiated SH-SY5Y cells treated with glyceraldehyde to induce Tau hyperphosphorylation, and subsequently neurite degeneration and cell death. Testing of such compounds on the newly developed model revealed an overall improvement of the induced defects by inhibition of AChE alone, showing a reduction of S396 aberrant phosphorylation along with a moderate amelioration of the neuron-like morphology. Finally, simultaneous AChE/GSK3 inhibition further enhanced the limited effects observed by AChE inhibition alone, resulting in an improvement of all the key parameters, such as cell viability, morphology, and Tau abnormal phosphorylation. date: 2022-12-01 date_type: published publisher: MDPI official_url: https://doi.org/10.3390/ijms232314794 oa_status: green full_text_type: pub language: eng primo: open primo_central: open_green verified: verified_manual elements_id: 1995999 doi: 10.3390/ijms232314794 medium: Electronic pii: ijms232314794 lyricists_name: Uras, Giuseppe lyricists_id: GURAS33 actors_name: Flynn, Bernadette actors_id: BFFLY94 actors_role: owner funding_acknowledgements: [School of Pharmacy, The University of Nottingham, UK]; [China Scholarship Council, China]; [Erasmus+ programme, Italy] full_text_status: public publication: International Journal of Molecular Sciences volume: 23 number: 23 article_number: 14794 pages: 18 event_location: Switzerland issn: 1661-6596 citation: Uras, Giuseppe; Li, Xinuo; Manca, Alessia; Pantaleo, Antonella; Bo, Marco; Xu, Jinyi; Allen, Stephanie; Uras, Giuseppe; Li, Xinuo; Manca, Alessia; Pantaleo, Antonella; Bo, Marco; Xu, Jinyi; Allen, Stephanie; Zhu, Zheying; - view fewer <#> (2022) Development of p-Tau Differentiated Cell Model of Alzheimer’s Disease to Screen Novel Acetylcholinesterase Inhibitors. International Journal of Molecular Sciences , 23 (23) , Article 14794. 10.3390/ijms232314794 <https://doi.org/10.3390/ijms232314794>. Green open access document_url: https://discovery.ucl.ac.uk/id/eprint/10184217/1/ijms-23-14794.pdf