Hughes, D; Gonzalez, D; Maegawa, G; Bernat, JA; Holida, M; Giraldo, P; Atta, MG; ... Goker-Alpan, O; + view all (2023) Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease. Genetics in Medicine , 25 (12) , Article 100968. 10.1016/j.gim.2023.100968. (In press). Green open access