Hughes, D;
Gonzalez, D;
Maegawa, G;
Bernat, JA;
Holida, M;
Giraldo, P;
Atta, MG;
... Goker-Alpan, O; + view all
(2023)
Long-term safety and efficacy of pegunigalsidase alfa: A multicenter 6-year study in adult patients with Fabry disease.
Genetics in Medicine
, 25
(12)
, Article 100968. 10.1016/j.gim.2023.100968.
(In press).