Hughes, Michael Paul; Nelvagal, Hemanth Ramesh; Coombe-Tennant, Oliver; Smith, Dave; Smith, Claire; Massaro, Giulia; Poupon-Bejuit, Laura; ... Rahim, Ahad Abdul; + view all (2023) A Novel Small NPC1 Promoter Enhances AAV-Mediated Gene Therapy in Mouse Models of Niemann–Pick Type C1 Disease. Cells , 12 (12) , Article 1619. 10.3390/cells12121619. Green open access