?url_ver=Z39.88-2004&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Ajournal&rft.aulast=Messina&rft.aufirst=M&rft.au=Messina%2C+M&rft.issn=1699-3993&rft.title=Drugs+of+Today&rft.pages=63-70&rft.date=1+February+2023&rft.issue=2&rft.atitle=Atidarsagene+autotemcel+for+metachromatic+leukodystrophy&rft.volume=59&rft.genre=article