Veys, Koenraad; Zadora, Ward; Hohenfellner, Katharina; Bockenhauer, Detlef; Janssen, Mirian CH; Niaudet, Patrick; Servais, Aude; ... Levtchenko, Elena; + view all (2023) Outcome of infantile nephropathic cystinosis depends on early intervention, not genotype: A multicenter sibling cohort study. Journal of Inherited Metabolic Disease , 46 (1) pp. 43-54. 10.1002/jimd.12562. Green open access