Mah, Jean K;
Clemens, Paula R;
Guglieri, Michela;
Smith, Edward C;
Finkel, Richard S;
Tulinius, Mar;
Nevo, Yoram;
... NorthStar UK Network and CINRG DNHS Investigators; + view all
(2022)
Efficacy and Safety of Vamorolone in Duchenne Muscular Dystrophy: A 30-Month Nonrandomized Controlled Open-Label Extension Trial.
JAMA Network Open
, 5
(1)
, Article e2144178. 10.1001/jamanetworkopen.2021.44178.