Campbell, C;
Barohn, RJ;
Bertini, E;
Chabrol, B;
Comi, GP;
Darras, BT;
Finkel, RS;
... Clinical Evaluator Training Groups, .; + view all
(2020)
Meta-analyses of ataluren randomized controlled trials in nonsense mutation Duchenne muscular dystrophy.
Journal of Comparative Effectiveness Research
, 9
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10.2217/cer-2020-0095.