Colasante, G;
Lignani, G;
Brusco, S;
Di Berardino, C;
Carpenter, J;
Giannelli, S;
Valassina, N;
... Broccoli, V; + view all
(2020)
dCas9-Based Scn1a Gene Activation Restores Inhibitory Interneuron Excitability and Attenuates Seizures in Dravet Syndrome Mice.
Molecular Therapy
, 28
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pp. 235-253.
10.1016/j.ymthe.2019.08.018.