Welsh, NJ;
Gewinner, CA;
Mistry, K;
Koglin, M;
Cooke, J;
Butler, M;
Powney, B;
... Schapira, AHV; + view all
(2019)
Functional assessment of glucocerebrosidase modulator efficacy in primary patient-derived macrophages is essential for drug development and patient stratification.
Haematologica
10.3324/haematol.2019.224717.
(In press).