eprintid: 10065950 rev_number: 16 eprint_status: archive userid: 608 dir: disk0/10/06/59/50 datestamp: 2019-01-16 10:16:33 lastmod: 2021-09-26 23:09:32 status_changed: 2019-01-16 10:16:33 type: article metadata_visibility: show creators_name: Sogorb-Esteve, A creators_name: Garcia-Ayllon, M-S creators_name: Llansola, M creators_name: Felipo, V creators_name: Blennow, K creators_name: Saez-Valero, J title: Inhibition of gamma-Secretase Leads to an Increase in Presenilin-1 ispublished: pub divisions: UCL divisions: B02 divisions: C07 divisions: D07 divisions: F86 keywords: Alzheimer’s disease, Presenilin-1, γ-Secretase inhibitor, Therapy note: © The Author(s) 2017. Open Access: This article is distributed under the terms of the Creative Commons Attribution 4.0 International License (http://creativecommons.org/licenses/by/4.0/), which permits unrestricted use, distribution, and reproduction in any medium, provided you give appropriate credit to the original author(s) and the source, provide a link to the Creative Commons license, and indicate if changes were made. abstract: γ-Secretase inhibitors (GSIs) are potential therapeutic agents for Alzheimer’s disease (AD); however, trials have proven disappointing. We addressed the possibility that γ-secretase inhibition can provoke a rebound effect, elevating the levels of the catalytic γ-secretase subunit, presenilin-1 (PS1). Acute treatment of SH-SY5Y cells with the GSI LY-374973 (N-[N-(3,5-difluorophenacetyl)-l-alanyl]-S-phenylglycine t-butyl ester, DAPT) augments PS1, in parallel with increases in other γ-secretase subunits nicastrin, presenilin enhancer 2, and anterior pharynx-defective 1, yet with no increase in messenger RNA expression. Over-expression of the C-terminal fragment (CTF) of APP, C99, also triggered an increase in PS1. Similar increases in PS1 were evident in primary neurons treated repeatedly (4 days) with DAPT or with the GSI BMS-708163 (avagacestat). Likewise, rats examined after 21 days administered with avagacestat (40 mg/kg/day) had more brain PS1. Sustained γ-secretase inhibition did not exert a long-term effect on PS1 activity, evident through the decrease in CTFs of APP and ApoER2. Prolonged avagacestat treatment of rats produced a subtle impairment in anxiety-like behavior. The rebound increase in PS1 in response to GSIs must be taken into consideration for future drug development. date: 2018-06 date_type: published publisher: SPRINGER official_url: https://doi.org/10.1007/s12035-017-0705-1 oa_status: green full_text_type: pub language: eng primo: open primo_central: open_green article_type_text: Article verified: verified_manual elements_id: 1601032 doi: 10.1007/s12035-017-0705-1 language_elements: English lyricists_name: Sogorb Esteve, Aitana lyricists_id: AASOG25 actors_name: Cuccu, Clara actors_id: CCCUC40 actors_role: owner full_text_status: public publication: Molecular Neurobiology volume: 55 number: 6 pagerange: 5047-5058 pages: 12 issn: 1559-1182 citation: Sogorb-Esteve, A; Garcia-Ayllon, M-S; Llansola, M; Felipo, V; Blennow, K; Saez-Valero, J; (2018) Inhibition of gamma-Secretase Leads to an Increase in Presenilin-1. Molecular Neurobiology , 55 (6) pp. 5047-5058. 10.1007/s12035-017-0705-1 <https://doi.org/10.1007/s12035-017-0705-1>. Green open access document_url: https://discovery.ucl.ac.uk/id/eprint/10065950/1/Sogorb-Esteve2018_Article_InhibitionOf%CE%93-SecretaseLeadsTo.pdf