Cideciyan, AV;    Jacobson, SG;    Drack, AV;    Ho, AC;    Charng, J;    Garafalo, AV;    Roman, AJ;                                                                                 ... Russell, SR; + view all <#>        Cideciyan, AV;  Jacobson, SG;  Drack, AV;  Ho, AC;  Charng, J;  Garafalo, AV;  Roman, AJ;  Sumaroka, A;  Han, IC;  Hochstedler, MD;  Pfeifer, WL;  Sohn, EH;  Taiel, M;  Schwartz, MR;  Biasutto, P;  Wit, WD;  Cheetham, ME;  Adamson, P;  Rodman, DM;  Platenburg, G;  Tome, MD;  Balikova, I;  Nerinckx, F;  Zaeytijd, JD;  Van Cauwenbergh, C;  Leroy, BP;  Russell, SR;   - view fewer <#>    (2019)    Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect.                   Nature Medicine , 25    pp. 225-228.    10.1038/s41591-018-0295-0 <https://doi.org/10.1038/s41591-018-0295-0>.       Green open access