?url_ver=Z39.88-2004&rft_val_fmt=info%3Aofi%2Ffmt%3Akev%3Amtx%3Ajournal&rft.au=Cideciyan%2C+AV&rft.aufirst=AV&rft.aulast=Cideciyan&rft.pages=225-228&rft.date=February+2019&rft.volume=25&rft.atitle=Effect+of+an+intravitreal+antisense+oligonucleotide+on+vision+in+Leber+congenital+amaurosis+due+to+a+photoreceptor+cilium+defect&rft.title=Nature+Medicine&rft.genre=article