Shorrock, H;
van der Hoorn, D;
Boyd, P;
Hurtado, M;
Lamont, D;
Wirth, B;
Sleigh, JN;
... Gillingwater, TH; + view all
(2018)
UBA1/GARS-dependent pathways drive sensory-motor connectivity defects in spinal muscular atrophy.
Brain: A Journal of Neurology
, 141
(10)
pp. 2878-2894.
10.1093/brain/awy237.