Finkel, RS;
Mercuri, E;
Darras, BT;
Connolly, AM;
Kuntz, NL;
Kirschner, J;
Chiriboga, CA;
... De Vivo, DC; + view all
(2017)
Nusinersen versus Sham Control in Infantile-Onset Spinal Muscular Atrophy.
New England Journal of Medicine
, 377
(18)
pp. 1723-1732.
10.1056/NEJMoa1702752.