TY - JOUR JF - Neurology A1 - McCormack, M A1 - Gui, H A1 - Ingason, A A1 - Speed, D A1 - Wright, GEB A1 - Zhang, EJ A1 - Secolin, R A1 - Yasuda, C A1 - Kwok, M A1 - Wolking, S A1 - Becker, F A1 - Rau, S A1 - Avbersek, A A1 - Heggeli, K A1 - Leu, C A1 - Depondt, C A1 - Sills, GJ A1 - Marson, AG A1 - Auce, P A1 - Brodie, MJ A1 - Francis, B A1 - Johnson, MR A1 - Koeleman, BPC A1 - Striano, P A1 - Coppola, A A1 - Zara, F A1 - Kunz, WS A1 - Sander, JW A1 - Lerche, H A1 - Klein, KM A1 - Weckhuysen, S A1 - Krenn, M A1 - Gudmundsson, LJ A1 - Stefánsson, K A1 - Krause, R A1 - Shear, N A1 - Ross, CJD A1 - Delanty, N A1 - EPIGEN Consortium, . A1 - Pirmohamed, M A1 - Carleton, BC A1 - Canadian Pharmacogenomics Network for Drug Safety, . A1 - Cendes, F A1 - Lopes-Cendes, I A1 - Liao, W-P A1 - O'Brien, TJ A1 - Sisodiya, SM A1 - EpiPGX Consortium, . A1 - Cherny, S A1 - Kwan, P A1 - Baum, L A1 - ILAE-CGC, . A1 - Cavalleri, GL ID - discovery10041504 N2 - OBJECTIVE: To characterize, among European and Han Chinese populations, the genetic predictors of maculopapular exanthema (MPE), a cutaneous adverse drug reaction common to antiepileptic drugs. METHODS: We conducted a case-control genome-wide association study of autosomal genotypes, including Class I and II human leukocyte antigen (HLA) alleles, in 323 cases and 1,321 drug-tolerant controls from epilepsy cohorts of northern European and Han Chinese descent. Results from each cohort were meta-analyzed. RESULTS: We report an association between a rare variant in the complement factor H-related 4 (CFHR4) gene and phenytoin-induced MPE in Europeans (p = 4.5 × 10-11; odds ratio [95% confidence interval] 7 [3.2-16]). This variant is in complete linkage disequilibrium with a missense variant (N1050Y) in the complement factor H (CFH) gene. In addition, our results reinforce the association between HLA-A*31:01 and carbamazepine hypersensitivity. We did not identify significant genetic associations with MPE among Han Chinese patients. CONCLUSIONS: The identification of genetic predictors of MPE in CFHR4 and CFH, members of the complement factor H-related protein family, suggest a new link between regulation of the complement system alternative pathway and phenytoin-induced hypersensitivity in European-ancestral patients. SN - 1526-632X UR - https://doi.org/10.1212/WNL.0000000000004853 N1 - Copyright © 2017 The Author(s). This is an open access article distributed under the terms of the Creative Commons Attribution License 4.0 (CC BY) (http://creativecommons.org/licenses/by/4.0/), which permits unrestricted use, distribution, and reproduction in any medium, provided the original work is properly cited. IS - 4 TI - Genetic variation in CFH predicts phenytoin-induced maculopapular exanthema in European-descent patients EP - e341 AV - public SP - e332 VL - 90 Y1 - 2018/01/23/ ER -