%0 Journal Article %@ 1526-632X %A McCormack, M %A Gui, H %A Ingason, A %A Speed, D %A Wright, GEB %A Zhang, EJ %A Secolin, R %A Yasuda, C %A Kwok, M %A Wolking, S %A Becker, F %A Rau, S %A Avbersek, A %A Heggeli, K %A Leu, C %A Depondt, C %A Sills, GJ %A Marson, AG %A Auce, P %A Brodie, MJ %A Francis, B %A Johnson, MR %A Koeleman, BPC %A Striano, P %A Coppola, A %A Zara, F %A Kunz, WS %A Sander, JW %A Lerche, H %A Klein, KM %A Weckhuysen, S %A Krenn, M %A Gudmundsson, LJ %A Stefánsson, K %A Krause, R %A Shear, N %A Ross, CJD %A Delanty, N %A EPIGEN Consortium, . %A Pirmohamed, M %A Carleton, BC %A Canadian Pharmacogenomics Network for Drug Safety, . %A Cendes, F %A Lopes-Cendes, I %A Liao, W-P %A O'Brien, TJ %A Sisodiya, SM %A EpiPGX Consortium, . %A Cherny, S %A Kwan, P %A Baum, L %A ILAE-CGC, . %A Cavalleri, GL %D 2018 %F discovery:10041504 %J Neurology %N 4 %P e332-e341 %T Genetic variation in CFH predicts phenytoin-induced maculopapular exanthema in European-descent patients %U https://discovery.ucl.ac.uk/id/eprint/10041504/ %V 90 %X OBJECTIVE: To characterize, among European and Han Chinese populations, the genetic predictors of maculopapular exanthema (MPE), a cutaneous adverse drug reaction common to antiepileptic drugs. METHODS: We conducted a case-control genome-wide association study of autosomal genotypes, including Class I and II human leukocyte antigen (HLA) alleles, in 323 cases and 1,321 drug-tolerant controls from epilepsy cohorts of northern European and Han Chinese descent. Results from each cohort were meta-analyzed. RESULTS: We report an association between a rare variant in the complement factor H-related 4 (CFHR4) gene and phenytoin-induced MPE in Europeans (p = 4.5 × 10-11; odds ratio [95% confidence interval] 7 [3.2-16]). This variant is in complete linkage disequilibrium with a missense variant (N1050Y) in the complement factor H (CFH) gene. In addition, our results reinforce the association between HLA-A*31:01 and carbamazepine hypersensitivity. We did not identify significant genetic associations with MPE among Han Chinese patients. CONCLUSIONS: The identification of genetic predictors of MPE in CFHR4 and CFH, members of the complement factor H-related protein family, suggest a new link between regulation of the complement system alternative pathway and phenytoin-induced hypersensitivity in European-ancestral patients. %Z Copyright © 2017 The Author(s). This is an open access article distributed under the terms of the Creative Commons Attribution License 4.0 (CC BY) (http://creativecommons.org/licenses/by/4.0/), which permits unrestricted use, distribution, and reproduction in any medium, provided the original work is properly cited.